EligibleTrials

autologous bone marrow derived CD34+ HSPCs electroporated with BCL11A enhancer targeting Cas9 ribonucleoprotein: clinical trials recruiting now

Fewer than 3 recruiting trials found.

1
Recruiting trials
4
Conditions studied
1
US states with sites
1
Countries

Phase breakdown

Phase 1 1

Conditions being studied

ConditionTrials
Beta-Thalassemia1
Sickle Cell Anemia (HbSS, or HbSβ-thalassemia0)1
Sickle Cell Disease1
Transfusion Dependent Beta-Thalassaemia1

Recruiting trials involving autologous bone marrow derived CD34+ HSPCs electroporated with BCL11A enhancer targeting Cas9 ribonucleoprotein

Common questions

How many recruiting trials involve autologous bone marrow derived CD34+ HSPCs electroporated with BCL11A enhancer targeting Cas9 ribonucleoprotein?

1 recruiting trial across 4 conditions.

Is this list of trials complete?

No. For the full record, search ClinicalTrials.gov.

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